Best Biotech Stocks
200 stocks · Updated Sep 1, 2026
Top biotech stocks ranked by market cap.
| # | Stock | Symbol | Company | Price | Change % | Market Cap | Rev Growth | P/E | Sector |
|---|---|---|---|---|---|---|---|---|---|
| 1 | VRTXVertex Pharmaceuticals Incorporated | VRTX | Vertex Pharmaceuticals Incorporated | $548.11 | +0.66% | $138.98B | +7.82% | 32.26 | Healthcare |
| 2 | REGNRegeneron Pharmaceuticals, Inc. | REGN | Regeneron Pharmaceuticals, Inc. | $820.73 | +2.71% | $85.35B | +19.04% | 19.51 | Healthcare |
| 3 | MRNAModerna, Inc. | MRNA | Moderna, Inc. | $149.32 | +6.40% | $56.65B | +263.55% | -6.55 | Healthcare |
| 4 | ARGXargenx SE | ARGX | argenx SE | $1024.31 | -0.71% | $45.82B | — | 42.42 | Healthcare |
| 5 | RVMDRevolution Medicines, Inc. | RVMD | Revolution Medicines, Inc. | $208.23 | +1.29% | $44.98B | — | -24.34 | Healthcare |
| 6 | ALNYAlnylam Pharmaceuticals, Inc. | ALNY | Alnylam Pharmaceuticals, Inc. | $242.28 | +0.66% | $31.58B | +96.43% | 57.24 | Healthcare |
| 7 | ROIVRoivant Sciences Ltd. | ROIV | Roivant Sciences Ltd. | $34.52 | -0.36% | $27.15B | -77.83% | -23.91 | Healthcare |
| 8 | INSMInsmed Incorporated | INSM | Insmed Incorporated | $120.60 | -1.00% | $26.31B | +229.62% | -22.58 | Healthcare |
| 9 | INCYIncyte Corporation | INCY | Incyte Corporation | $123.89 | +0.54% | $25.89B | +20.87% | 17.45 | Healthcare |
| 10 | BNTXBioNTech SE | BNTX | BioNTech SE | $100.37 | -1.22% | $24.56B | — | -18.61 | Healthcare |
| 11 | UTHRUnited Therapeutics Corporation | UTHR | United Therapeutics Corporation | $513.67 | +0.65% | $22.41B | +7.38% | 18.36 | Healthcare |
| 12 | GMABGenmab A/S | GMAB | Genmab A/S | $33.24 | +0.26% | $16.79B | — | 4.20 | Healthcare |
| 13 | JAZZJazz Pharmaceuticals plc | JAZZ | Jazz Pharmaceuticals plc | $245.61 | -2.02% | $15.77B | +19.05% | 2288.73 | Healthcare |
| 14 | NBIXNeurocrine Biosciences, Inc. | NBIX | Neurocrine Biosciences, Inc. | $156.03 | +1.30% | $15.68B | +28.33% | 32.99 | Healthcare |
| 15 | BBIOBridgeBio Pharma, Inc. | BBIO | BridgeBio Pharma, Inc. | $76.49 | -0.13% | $15.41B | +54.84% | -18.84 | Healthcare |
| 16 | ASNDAscendis Pharma A/S | ASND | Ascendis Pharma A/S | $259.81 | -1.23% | $14.73B | — | -51.06 | Healthcare |
| 17 | EXELExelixis, Inc. | EXEL | Exelixis, Inc. | $56.04 | +2.56% | $13.89B | +5.63% | 18.59 | Healthcare |
| 18 | BMRNBioMarin Pharmaceutical Inc. | BMRN | BioMarin Pharmaceutical Inc. | $64.71 | -0.80% | $12.62B | +17.03% | 36.46 | Healthcare |
| 19 | MDGLMadrigal Pharmaceuticals, Inc. | MDGL | Madrigal Pharmaceuticals, Inc. | $537.85 | -0.40% | $12.56B | +126.84% | -40.21 | Healthcare |
| 20 | HALOHalozyme Therapeutics, Inc. | HALO | Halozyme Therapeutics, Inc. | $107.47 | +0.92% | $12.50B | +51.60% | 42.59 | Healthcare |
| 21 | ARWRArrowhead Pharmaceuticals, Inc. | ARWR | Arrowhead Pharmaceuticals, Inc. | $82.41 | -0.04% | $12.48B | -86.41% | 51.38 | Healthcare |
| 22 | SMMTSummit Therapeutics Inc. | SMMT | Summit Therapeutics Inc. | $14.29 | +4.94% | $11.43B | — | -14.72 | Healthcare |
| 23 | TECHBio-Techne Corporation | TECH | Bio-Techne Corporation | $72.25 | -0.08% | $11.35B | -0.39% | 141.79 | Healthcare |
| 24 | AXSMAxsome Therapeutics, Inc. | AXSM | Axsome Therapeutics, Inc. | $203.90 | +2.71% | $10.61B | +57.42% | -51.14 | Healthcare |
| 25 | KRYSKrystal Biotech, Inc. | KRYS | Krystal Biotech, Inc. | $360.83 | +0.41% | $10.54B | +31.95% | 48.09 | Healthcare |
| 26 | IONSIonis Pharmaceuticals, Inc. | IONS | Ionis Pharmaceuticals, Inc. | $60.27 | -0.14% | $10.15B | +86.98% | -30.52 | Healthcare |
| 27 | KYMRKymera Therapeutics, Inc. | KYMR | Kymera Therapeutics, Inc. | $117.62 | -1.00% | $9.72B | +55.50% | -22.72 | Healthcare |
| 28 | CYTKCytokinetics, Incorporated | CYTK | Cytokinetics, Incorporated | $71.85 | +1.33% | $9.69B | +1125.78% | -9.43 | Healthcare |
| 29 | PRAXPraxis Precision Medicines, Inc. | PRAX | Praxis Precision Medicines, Inc. | $349.69 | -0.17% | $9.61B | -100.00% | -23.89 | Healthcare |
| 30 | PTGXProtagonist Therapeutics, Inc. | PTGX | Protagonist Therapeutics, Inc. | $146.02 | -1.17% | $9.28B | -100.00% | -49.44 | Healthcare |
| 31 | PCVXVaxcyte, Inc. | PCVX | Vaxcyte, Inc. | $60.93 | +0.31% | $8.64B | — | -10.43 | Healthcare |
| 32 | IMVTImmunovant, Inc. | IMVT | Immunovant, Inc. | $39.45 | -3.36% | $8.50B | — | -10.55 | Healthcare |
| 33 | IBRXImmunityBio, Inc. | IBRX | ImmunityBio, Inc. | $7.86 | -1.13% | $8.43B | +406.95% | -19.60 | Healthcare |
| 34 | APGEApogee Therapeutics, Inc. | APGE | Apogee Therapeutics, Inc. | $135.07 | -0.01% | $8.35B | — | -20.25 | Healthcare |
| 35 | TGTXTG Therapeutics, Inc. | TGTX | TG Therapeutics, Inc. | $55.10 | +1.47% | $8.26B | +69.56% | 18.79 | Healthcare |
| 36 | SYRESpyre Therapeutics, Inc. | SYRE | Spyre Therapeutics, Inc. | $88.10 | -1.38% | $7.85B | — | -153.02 | Healthcare |
| 37 | RYTMRhythm Pharmaceuticals, Inc. | RYTM | Rhythm Pharmaceuticals, Inc. | $104.55 | -1.49% | $7.35B | +83.81% | -28.64 | Healthcare |
| 38 | CAICaris Life Sciences, Inc. | CAI | Caris Life Sciences, Inc. | $24.81 | -2.67% | $7.25B | +78.78% | -452.83 | Healthcare |
| 39 | ABVXAbivax S.A. | ABVX | Abivax S.A. | $113.42 | +1.51% | $7.19B | — | -19.77 | Healthcare |
| 40 | SRRKScholar Rock Holding Corporation | SRRK | Scholar Rock Holding Corporation | $55.45 | -2.38% | $6.93B | — | -14.18 | Healthcare |
| 41 | BLTEBelite Bio, Inc | BLTE | Belite Bio, Inc | $155.10 | -0.39% | $6.72B | — | -68.59 | Healthcare |
| 42 | CGONCG Oncology Inc. | CGON | CG Oncology Inc. | $74.94 | -0.29% | $6.56B | +1982.69% | -31.47 | Healthcare |
| 43 | ERASErasca, Inc. | ERAS | Erasca, Inc. | $16.86 | -5.68% | $6.26B | — | -22.54 | Healthcare |
| 44 | TVTXTravere Therapeutics, Inc. | TVTX | Travere Therapeutics, Inc. | $65.70 | -0.87% | $6.11B | +55.63% | -73.46 | Healthcare |
| 45 | MIRMMirum Pharmaceuticals, Inc. | MIRM | Mirum Pharmaceuticals, Inc. | $99.11 | +1.08% | $5.94B | -100.00% | -201.97 | Healthcare |
| 46 | COGTCogent Biosciences, Inc. | COGT | Cogent Biosciences, Inc. | $34.37 | -1.81% | $5.92B | — | -7.47 | Healthcare |
| 47 | DNTHDianthus Therapeutics, Inc. | DNTH | Dianthus Therapeutics, Inc. | $106.52 | +0.86% | $5.92B | -100.00% | 112.19 | Healthcare |
| 48 | PTCTPTC Therapeutics, Inc. | PTCT | PTC Therapeutics, Inc. | $70.11 | +0.82% | $5.85B | -76.83% | 8.58 | Healthcare |
| 49 | XENEXenon Pharmaceuticals Inc. | XENE | Xenon Pharmaceuticals Inc. | $59.85 | -0.61% | $5.80B | -100.00% | -12.49 | Healthcare |
| 50 | LGNDLigand Pharmaceuticals Incorporated | LGND | Ligand Pharmaceuticals Incorporated | $284.87 | +0.27% | $5.62B | +14.09% | 38.46 | Healthcare |
Showing 1-50 of 200 stocks
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Frequently Asked Questions
How is the "Best Biotech Stocks" list created?
This list is screened using the criteria: industry ILIKE '%biotech%', market_cap DESC. Data is refreshed daily from market sources.
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Stock data is updated daily. Intraday signals like top gainers are refreshed every 5 minutes during market hours.
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